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MPS/Sanfilippo Syndrome, special needs 1/26/15 MPS/Sanfilippo Syndrome, special needs 1/26/15 taking out the trash: a garbage lesson on Sanfilippo Read More
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MPS/Sanfilippo Syndrome 4/21/14 MPS/Sanfilippo Syndrome 4/21/14 updates regarding gene therapy, please read and share Read More
MPS/Sanfilippo Syndrome 4/17/14 MPS/Sanfilippo Syndrome 4/17/14 A [potential] cure for Sanfilippo is here! Read More